Fondazione Cariplo and Fondazione Telethon: 21 projects funded with 5 million euros for basic research in rare diseases

The best projects of the 2022 call for basic research from all over Italy to study still obscure portions of our genetic heritage have been funded. The collaboration between Fondazione Cariplo and Fondazione Telethon continues: 21 new basic research projects have been funded for a total of about 5 million euros. The goal of the […]

Margaux discovering the world thanks to gene therapy

She was the first Belgian girl with the rare immunodeficiency ADA-SCID treated with the gene therapy approach developed by Telethon researchers. From the risk of a life of seclusion, she has conquered the possibility of doing whatever she likes.

Osteopetrosis: new opportunity of treatment thanks to a licensing agreement

SiSaf announces a research collaboration and licensing agreement with the University of L’Aquila for the treatment of the debilitating bone disease, Autosomal Dominant Osteopetrosis Type 2.